Gene Therapy Helps Cure Children with a Form of Bubble Boy Disease

By David Wolf, Attorney
Published by Child Injury Lawyer Network

Bubble Boy disease is the term used to describe a medical condition called severe combined immunodeficiency, or SCID. It is a relatively rare disease in that forty to one hundred people are diagnosed with the disease per year in the United States. It is a genetic disorder that affects and compromises a person’s immune system. Patients were give gene therapy and results indicate that eight of the patients were successfully treated according to a study reported in the New England Journal of Medicine. You can read more about this study which gives some hope to children and families dealing with this disease at Study – Gene Therapy Cures 8 Children with Bubble Boy Disease.